Recruiting Gaucher Disease Studies in Durham
About Gaucher Disease Clinical Trials in Durham
Gaucher disease is an inherited metabolic disorder caused by deficiency of the enzyme glucocerebrosidase, leading to accumulation of fatty substances in organs. It is the most common lysosomal storage disorder. Treatment includes enzyme replacement therapy and substrate reduction therapy.
There are currently 1 gaucher disease clinical trials recruiting participants in Durham, NORTH%20CAROLINA. These studies are seeking a combined 15 participants. Research is being sponsored by Prevail Therapeutics. Clinical trial participation is free and participants receive study-related medical care at no cost.
Gaucher Disease Clinical Trials in Durham — FAQ
Are there gaucher disease clinical trials in Durham?
Yes, there are 1 gaucher disease clinical trials currently recruiting in Durham, NORTH%20CAROLINA. Browse the studies on this page to find one that fits.
How do I join a clinical trial in Durham?
Browse the studies listed above, click one that interests you, and complete the free eligibility form. A study coordinator at the Durham research site will contact you about next steps.
Are clinical trials in Durham free?
Yes, clinical trial participation is always free. Study-related treatment, medical tests, and doctor visits are provided at no cost. Many Durham studies also compensate for your time and travel.
What gaucher disease treatments are being tested?
The 1 active trials in Durham are testing new therapies including novel drugs, biologics, and treatment approaches for gaucher disease.
Data updated March 2, 2026 from ClinicalTrials.gov